بیماری لبر

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The first gene therapy for the treatment of rp

Phase 1 studies have shown potential benefit of gene replacement in RPE65-mediated inherited retinal dystrophy. This phase 3 study assessed the efficacy and safety of voretigene neparvovec in participants whose inherited retinal dystrophy would otherwise progress to complete blindness. Methods In this open-label, randomised, controlled phase 3 trial done at two sites in the USA, [...]

By |۱۳۹۶/۷/۲۲ ،۰۷:۴۲:۵۶ +۰۰:۰۰مهر ۲۲ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments