About iranrp

This author has not yet filled in any details.
So far iranrp has created 126 blog entries.

To Treat an Inherited Retinal Disease….

In simple terms, genes are like recipes for making proteins. All the cells in our bodies “read” genetic information so they can make the critical proteins necessary to stay healthy and function properly. If there is a mistake in a gene — that is, a misspelling — a protein might not be made correctly and [...]

By |۱۳۹۶/۸/۹ ،۰۶:۴۷:۴۳ +۰۰:۰۰آبان ۹ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

FDA Unanimously Recommends Approval for Spark’s RPE65

FDA Committee Unanimously Recommends Approval for Spark’s RPE65 Gene Therapy – Final Decision Due in January 2018 Spark Therapeutics has taken a major step closer to gaining marketing approval for its vision-restoring gene therapy for people with RPE65 mutations causing Leber congenital amaurosis (LCA) and retinitis pigmentosa. At the conclusion of a public hearing on [...]

By |۱۳۹۶/۷/۲۶ ،۰۹:۱۷:۴۴ +۰۰:۰۰مهر ۲۶ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

The first gene therapy for the treatment of rp

Phase 1 studies have shown potential benefit of gene replacement in RPE65-mediated inherited retinal dystrophy. This phase 3 study assessed the efficacy and safety of voretigene neparvovec in participants whose inherited retinal dystrophy would otherwise progress to complete blindness. Methods In this open-label, randomised, controlled phase 3 trial done at two sites in the USA, [...]

By |۱۳۹۶/۷/۲۲ ،۰۷:۴۲:۵۶ +۰۰:۰۰مهر ۲۲ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

A Change in Identity Might Someday Save Vision

A Change in Identity Might Someday Save Vision No, people with inherited retinal diseases don’t have to adopt new names or personas, or go into witness protection programs, to save their vision. But by changing the identity of cells in the retina — namely rods — researchers may someday be able to slow or halt [...]

By |۱۳۹۶/۷/۱۵ ،۱۱:۲۴:۵۷ +۰۰:۰۰مهر ۱۵ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

FFB Investing in Cures Summit

FFB’s Investments Are Filling the Pipeline for Vision-Saving Therapies With five gene-therapy clinical trials underway or soon to begin, Applied Genetic Technologies Corporation (AGTC) is generating tremendous excitement for the potential to overcome vision loss from several inherited retinal diseases. At the Foundation’s Investing in Cures Summit on September 16 in Chicago, Sue Washer, AGTC’s [...]

By |۱۳۹۶/۷/۱۲ ،۱۱:۲۵:۳۸ +۰۰:۰۰مهر ۱۲ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

A Spice for the Eyes

Turmeric, also known as “the golden spice,” has been around for more than 4,000 years. In India, where Radha Ayyagari, Ph.D., grew up, it’s used widely as both a food spice and an herbal medicine for treating a variety of diseases, including cancer, arthritis, urinary-tract infections and digestive disorders. It has been scientifically established that [...]

By |۱۳۹۶/۷/۱ ،۰۶:۲۳:۳۴ +۰۰:۰۰مهر ۱ام, ۱۳۹۶|English, دسته‌بندی نشده|0 Comments

Nine Promising Translational Research Efforts By FFB

FFB-Funded Scientists Report on Nine Promising Translational Research Efforts By Ben Shaberman on July 24, 2017 | 0 Comments Translational research — moving promising science out of laboratories and into clinical trials — is essential to getting vision-saving, retinal-disease treatments out to the millions who need them. With that said, translational research is also costly [...]

By |۱۳۹۶/۶/۳۰ ،۰۵:۴۴:۰۲ +۰۰:۰۰شهریور ۱۱ام, ۱۳۹۶|English|0 Comments

Develop a Vision-Restoring System that Connects to the Brain

Scientists Receive $25 Million to Develop a Vision-Restoring System that Connects to the Brain By Ben Shaberman on July 26, 2017 While researchers around the world are developing numerous drugs and biological therapies for ocular diseases and injuries, an international scientific team coordinated in France is developing an innovative approach to bring back eyesight to [...]

By |۱۳۹۶/۶/۳۰ ،۰۵:۴۴:۱۸ +۰۰:۰۰شهریور ۲ام, ۱۳۹۶|English|0 Comments

FFB-Casey Innovation

Forty-Four High-Impact Retinal-Research Efforts Highlighted at FFB-Casey Innovation Summit By Ben Shaberman on May 23, 2017 For anyone wanting to know about the latest clinically focused research for inherited retinal diseases (IRDs), the Innovation Summit for Retinal Cell and Gene Therapy was the place to be. In its fourth year, the meeting is becoming the [...]

By |۱۳۹۶/۶/۳۰ ،۰۵:۴۴:۳۵ +۰۰:۰۰مرداد ۲۸ام, ۱۳۹۶|English|0 Comments

FFB Convenes Experts to Discuss Therapeutic Opportunities for Stargardt Disease

By Ben Shaberman on February 28, 2017 Stargardt disease is the world’s leading cause of inherited macular degeneration, affecting 30,000 people in the United States alone. It is also a challenging condition to understand and treat. While Stargardt disease often causes severe loss of central eyesight, its effect on vision and the retina can vary [...]

By |۱۳۹۶/۶/۳۰ ،۰۵:۴۴:۵۲ +۰۰:۰۰تیر ۲۱ام, ۱۳۹۶|English|0 Comments