In simple terms, genes are like recipes for making proteins. All the cells in our bodies “read” genetic information so they can make the critical proteins necessary to stay healthy and function properly. If there is a mistake in a gene — that is, a misspelling — a protein might not be made correctly and [...]
FFB’s Investments Are Filling the Pipeline for Vision-Saving Therapies With five gene-therapy clinical trials underway or soon to begin, Applied Genetic Technologies Corporation (AGTC) is generating tremendous excitement for the potential to overcome vision loss from several inherited retinal diseases. At the Foundation’s Investing in Cures Summit on September 16 in Chicago, Sue Washer, AGTC’s [...]
