بیماری لبر

/برچسب: بیماری لبر

The first gene therapy for the treatment of rp

Phase 1 studies have shown potential benefit of gene replacement in RPE65-mediated inherited retinal dystrophy. This phase 3 study assessed the efficacy and safety of voretigene neparvovec in participants whose inherited retinal dystrophy would otherwise progress to complete blindness. Methods In this open-label, randomised, controlled phase 3 trial done at two sites in the USA, [...]

به وسیله |2017-10-14T11:12:56+03:30اکتبر 14th, 2017|English, دسته‌بندی نشده|بدون دیدگاه