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To Treat an Inherited Retinal Disease….

In simple terms, genes are like recipes for making proteins. All the cells in our bodies “read” genetic information so they can make the critical proteins necessary to stay healthy and function properly. If there is a mistake in a gene — that is, a misspelling — a protein might not be made correctly and [...]

به وسیله |۱۳۹۶/۸/۹ ،۱۰:۱۷:۴۳ +۰۰:۰۰آبان ۹ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه

FDA Unanimously Recommends Approval for Spark’s RPE65

FDA Committee Unanimously Recommends Approval for Spark’s RPE65 Gene Therapy – Final Decision Due in January 2018 Spark Therapeutics has taken a major step closer to gaining marketing approval for its vision-restoring gene therapy for people with RPE65 mutations causing Leber congenital amaurosis (LCA) and retinitis pigmentosa. At the conclusion of a public hearing on [...]

به وسیله |۱۳۹۶/۷/۲۶ ،۱۲:۴۷:۴۴ +۰۰:۰۰مهر ۲۶ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه

The first gene therapy for the treatment of rp

Phase 1 studies have shown potential benefit of gene replacement in RPE65-mediated inherited retinal dystrophy. This phase 3 study assessed the efficacy and safety of voretigene neparvovec in participants whose inherited retinal dystrophy would otherwise progress to complete blindness. Methods In this open-label, randomised, controlled phase 3 trial done at two sites in the USA, [...]

به وسیله |۱۳۹۶/۷/۲۲ ،۱۱:۱۲:۵۶ +۰۰:۰۰مهر ۲۲ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه

A Change in Identity Might Someday Save Vision

A Change in Identity Might Someday Save Vision No, people with inherited retinal diseases don’t have to adopt new names or personas, or go into witness protection programs, to save their vision. But by changing the identity of cells in the retina — namely rods — researchers may someday be able to slow or halt [...]

به وسیله |۱۳۹۶/۷/۱۵ ،۱۴:۵۴:۵۷ +۰۰:۰۰مهر ۱۵ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه

FFB Investing in Cures Summit

FFB’s Investments Are Filling the Pipeline for Vision-Saving Therapies With five gene-therapy clinical trials underway or soon to begin, Applied Genetic Technologies Corporation (AGTC) is generating tremendous excitement for the potential to overcome vision loss from several inherited retinal diseases. At the Foundation’s Investing in Cures Summit on September 16 in Chicago, Sue Washer, AGTC’s [...]

به وسیله |۱۳۹۶/۷/۱۲ ،۱۴:۵۵:۳۸ +۰۰:۰۰مهر ۱۲ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه

A Spice for the Eyes

Turmeric, also known as “the golden spice,” has been around for more than 4,000 years. In India, where Radha Ayyagari, Ph.D., grew up, it’s used widely as both a food spice and an herbal medicine for treating a variety of diseases, including cancer, arthritis, urinary-tract infections and digestive disorders. It has been scientifically established that [...]

به وسیله |۱۳۹۶/۷/۱ ،۰۹:۵۳:۳۴ +۰۰:۰۰مهر ۱ام, ۱۳۹۶|English, دسته‌بندی نشده|بدون دیدگاه